PNH is a chronic, devastating, and potentially life-threatening disease characterized by uncontrolled terminal complement–mediated attack on red and white blood cells and platelets that can lead to severe consequences of thrombosis, organ damage, and early mortality.1
MORTALITY
Up to 35%
of patients with PNH die within 6 years despite historical supportive care.
aHistorical supportive care included blood transfusion, anticoagulation, immunosuppressive therapy, corticosteroids, and bone marrow transplantation.2,3
bRetrospective 6-year survival in historical control patients diagnosed with PNH between 1985 and 2005 in France (N=100). Retrospective thrombosis data presented are also from historical control group (N=44).3
cFive-year survival in patients diagnosed with PNH between 1997 and 2004 in Leeds, UK (N=30).2
Fatigue is one of the most recognizable symptoms of PNH. But PNH is much more than one symptom, and the ongoing hemolysis that characterizes this disease can have devastating consequences, including thrombosis.1,6,7
*Actor portrayal. Each person’s experience with PNH may vary. Quotes are composites based on actual experiences of real people living with PNH.
Patients struggle with both the physical and mental toll of this disease.6
Dr Hill explains what causes this rare disease, how part of your body’s own immune system plays a role, and certain complications to look out for.8-11.